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Show them a world beyond PNH.

Choose FABHALTA—a groundbreaking treatment that helps deliver substantial Hb improvements in both C5i-experienced and complement inhibitor–naive adults with PNH

Groundbreaking Hb improvements with the first and only FDA-approved oral monotherapy for adults with PNH1 

  • APPLY primary end points (FABHALTA vs C5is [eculizumab or ravulizumab]): response rates for sustained Hb increase of ≥2 g/dL: 82.3% (N=62) vs 0% (N=35) with C5is (difference: 81.5; 95% CI, 71.6-91.4; P<0.0001). Response rates for sustained Hb of ≥12 g/dL: 67.7% (N=62) vs 0% (N=35) with C5is (difference: 66.6; 95% CI, 54.6-78.6; P<0.0001). Differences reflect an adjusted difference in proportion

  • APPOINT single-arm study primary end point: response rates for sustained Hb increase ≥2 g/dL: 77.5% (N=40; 95% CI, 61.5-89.2)

  • All primary end points were measured in the absence of RBC transfusions after 24 weeks

Learn more about FABHALTA data in C5i-experienced and complement inhibitor–naive patients

FABHALTA is an FDA-approved treatment for adults with PNH. FABHALTA has displayed efficacy in C5i-experienced and complement inhibitor–naive patients with PNH.1 

FABHALTA (Fab-HALT-ah) describes a Factor B inhibitor (FAB) of the alternative pathway (ALTA) of the complement system.1

Discover how FABHALTA works

See the efficacy results for FABHALTA

Explore the safety profile for FABHALTA

See how adult patients take FABHALTA

Definitions 
C5i, C5 inhibitor; Hb, hemoglobin; PNH, paroxysmal nocturnal hemoglobinuria; RBC, red blood cell. 

Reference 
1. Fabhalta. Prescribing information. Novartis Pharmaceuticals Corp.